In a bold attempt to halt the progression of some cases of Alzheimer’s disease, a group of researchers are trying something new: injecting a protective gene into patients’ brains. The trial only involved five patients with a particular genetic risk for Alzheimer’s disease. They received a very low dose of gene therapy – a safety …
Promising trial targets genetic risk for Alzheimer’s disease Read More »
In a bold attempt to halt the progression of some cases of Alzheimer’s disease, a group of researchers are trying something new: injecting a protective gene into patients’ brains. The trial only involved five patients with a particular genetic risk for Alzheimer’s disease. They received a very low dose of gene therapy – a safety …
Promising trial targets genetic risk for Alzheimer’s disease Read More »
Treatment of glutaric aciduria type I (GA-I) by intracerebroventricular administration of GCDH. Credit: Institute of Zoology, Chinese Academy of Sciences, China Glutaric aciduria type I (GA-I) is an inherited disease caused by a mutation in the glutaryl-CoA dehydrogenase (GCDH) gene. The global incidence of GA-I is estimated at 1/100,000, with approximately 75,000 cases worldwide. Patients …
Promising study suggests AAV-based gene therapy can treat type I glutaric aciduria Read More »
Treatment of glutaric aciduria type I (GA-I) by intracerebroventricular administration of GCDH. Credit: Institute of Zoology, Chinese Academy of Sciences, China Glutaric aciduria type I (GA-I) is an inherited disease caused by a mutation in the glutaryl-CoA dehydrogenase (GCDH) gene. The global incidence of GA-I is estimated at 1/100,000, with approximately 75,000 cases worldwide. Patients …
Promising study suggests AAV-based gene therapy can treat type I glutaric aciduria Read More »
